Pfizer Licenses Spinal Muscular Atrophy Program From Repligen

In August, Repligen decided to get out of the drug discovery business and focus on manufacturing biologic drugs, so it wasn't a big surprise today when the company announced that it had licensed its spinal muscular atrophy, or SMA, program to Pfizer .

The SMA program includes a phase 1 drug candidate, RG3039, as well as backup compounds and enabling technologies. Repligen licensed the program from Families of SMA, a charity that offers support to families and researchers developing drugs to treat the disease. SMA is a neurodegenerative genetic disease that affects approximately one in 6,000 babies.

Repligen will get $5 million upfront and potentially another $65 million if future milestones are met. Pfizer also owes Repligen undisclosed royalties on any future sales of SMA drugs developed under the agreement.


Repligen will complete the first two cohorts of healthy volunteers in the ongoing phase I trial of RG3039, and then Pfizer will take over development of the program.

link

The article Pfizer Licenses Spinal Muscular Atrophy Program From Repligen originally appeared on Fool.com.

Fool contributor Brian Orelli has no positions in the stocks mentioned above. The Motley Fool has no positions in the stocks mentioned above. Try any of our Foolish newsletter services free for 30 days. We Fools may not all hold the same opinions, but we all believe that considering a diverse range of insights makes us better investors. The Motley Fool has a disclosure policy.

Copyright © 1995 - 2013 The Motley Fool, LLC. All rights reserved. The Motley Fool has a disclosure policy.


Increase your money and finance knowledge from home

Income Investing

Grow your nest-egg.

View Course »

Understanding Stock Market Indexes

What does it mean when people say "the market is up 2%"?

View Course »

Add a Comment

*0 / 3000 Character Maximum